Brochure

RNA Therapeutics and Gene Therapy Platform

Biocytogen provides cutting-edge gene-edited and humanized mouse models to support RNA therapeutics and gene therapy research across a wide range of diseases. Our integrated platforms enable efficient in vitro and in vivo evaluation of therapeutic efficacy, safety, and immunogenicity—streamlining preclinical studies and IND applications.

RNA Therapeutics and Gene Therapy Platform
October 18, 2025
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Oligonucleotide Drugs

  • Introduction
  • Evaluation Platforms for Oligonucleotide Drugs
    • Obesity and Type 2 Diabetes
    • Hyperlipidemia and Related Diseases
    • Liver Diseases
    • Pulmonary Diseases
    • Neurological Diseases

mRNA Therapeutics

  • Introduction
  • mRNA Drugs
  • mRNA Vaccines

Gene Therapy

  • Introduction
  • Animal Models for Gene Therapy
    • Duchenne Muscular Dystrophy
    • Inherited Retinal Disease
    • Hemophilia

Lipid Nanoparticle (LNP) Delivery System

Blood–Brain Barrier Crossing Strategies

Pharmacology Platform Capabilities